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Compassionate Use

Showing 1 - 25 of >10,000

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LOCATIONS

Trial (Vidutolimod)

Available
    • (no location specified)
    Sep 25, 2023

    COVID-19 Trial (VYD222)

    No longer available
    • COVID-19
    • (no location specified)
    Aug 18, 2023

    Pantothenate Kinase-Associated Neurodegeneration Trial (Deferiprone)

    No longer available
    • Pantothenate Kinase-Associated Neurodegeneration
    • (no location specified)
    Nov 9, 2022

    Diabetes, Lipodystrophy, Hyperlipidemia Trial run by the NIDDK (Metreleptin)

    Active, not recruiting
    • Diabetes
    • +2 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 21, 2023

    Lymphangioma Trial in Albuquerque (Alpelisib)

    Available
    • Lymphangioma
    • Albuquerque, New Mexico
      University of New Mexico - Cancer Center
    Oct 4, 2022

    Lipodystrophy, Diabetes, Hyperlipidemia Trial run by the NIDDK (Metreleptin)

    Recruiting
    • Lipodystrophy
    • +2 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Jan 23, 2023

    Colitis, Ulcerative Trial (Etrasimod)

    Available
    • Colitis, Ulcerative
    • (no location specified)
    Aug 29, 2023

    Alzheimer Trial (TB006)

    Available
    • Alzheimer Disease
    • (no location specified)
    Jul 14, 2023

    Pruritus Trial (Linerixibat)

    Available
    • Pruritus
    • (no location specified)
    Jul 1, 2022

    Sarcoma,Soft Tissue, Gynecologic Cancer Trial (AL3818)

    Available
    • Sarcoma,Soft Tissue
    • Gynecologic Cancer
    • (no location specified)
    Nov 22, 2022

    Epilepsy Trial (Brivaracetam)

    Available
    • Epilepsy
    • (no location specified)
    Jun 7, 2022

    Pseudoaneurysm, Carotid, Pseudoaneurysm Trial in Miami (PK Papyrus)

    Temporarily not available
    • Pseudoaneurysm, Carotid
    • Pseudoaneurysm
    • PK Papyrus
    • Miami, Florida
      Jackson Memorial Hospital
    Jun 21, 2022

    HIV Trial (Fostemsavir)

    Available
    • HIV Infections
    • (no location specified)
    Jun 13, 2022

    Metachromatic Leukodystrophy Trial in Durham (Enriched Hematopoetic Stem Cell Infusion)

    No longer available
    • Metachromatic Leukodystrophy
    • Enriched Hematopoetic Stem Cell Infusion
    • Durham, North Carolina
      Duke University
    Jul 15, 2022

    Renal Failure Trial in Chicago (Biological/Vaccine: Enriched Hematopoetic Stem Cell Infusion)

    No longer available
    • Renal Failure
    • Biological/Vaccine: Enriched Hematopoetic Stem Cell Infusion
    • Chicago, Illinois
      Northwestern Memorial Hospital
    Jul 15, 2022

    Bullous Pemphigoid Trial (dupilumab)

    Temporarily not available
    • Bullous Pemphigoid
    • (no location specified)
    Jun 7, 2023

    Sphingomyelin Lipidosis Trial (olipudase alfa (GZ402665))

    Approved for marketing
    • Sphingomyelin Lipidosis
    • olipudase alfa (GZ402665)
    • (no location specified)
    Sep 15, 2022

    Relapsed or Refractory (R/R) Follicular Lymphoma (FL), DLBCL (DLBCL) Trial (Odronextamab)

    Available
    • Relapsed or Refractory (R/R) Follicular Lymphoma (FL)
    • Diffuse Large B-Cell Lymphoma (DLBCL)
    • (no location specified)
    Nov 8, 2022

    GERD, Gastroesophageal Reflux, Gastroparesis Trial in Kansas City (Domperidone)

    Recruiting
    • GERD
    • +2 more
    • Kansas City, Missouri
      Children's Mercy Hospitals and Clinics
    May 17, 2022

    Paroxysmal Nocturnal Hemoglobinuria Trial (Pozelimab, Cemdisiran)

    Available
    • Paroxysmal Nocturnal Hemoglobinuria
    • (no location specified)
    Aug 31, 2023

    CD55-Deficient Protein-Losing Enteropathy Trial (Pozelimab)

    Available
    • CD55-Deficient Protein-Losing Enteropathy
    • (no location specified)
    Aug 14, 2023

    Malignant Tumor Trial (Experimental: DaRT seeds)

    Not yet recruiting
    • Malignant Tumor
    • Experimental: DaRT seeds
    • (no location specified)
    Mar 27, 2023

    Hyperkinetic Movement Disorders Trial (tetrabenazine)

    Available
    • Hyperkinetic Movement Disorders
    • (no location specified)
    Feb 19, 2022

    Glioblastoma, High Grade Glioma, Recurrent Glioblastoma Trial in Seoul (GX-I7)

    No longer available
    • Glioblastoma
    • +4 more
    • Seoul, Korea, Republic of
      Kangnam St. Mary's Hospital
    Mar 2, 2022

    Congenital Haemophilia Trial in United States (Concizumab)

    Available
    • Congenital Haemophilia
    • Chicago, Illinois
    • +9 more
    Jan 5, 2023