Compassionate Use
Showing 1 - 25 of >10,000
Pantothenate Kinase-Associated Neurodegeneration Trial (Deferiprone)
No longer available
- Pantothenate Kinase-Associated Neurodegeneration
- (no location specified)
Nov 9, 2022
Diabetes, Lipodystrophy, Hyperlipidemia Trial run by the NIDDK (Metreleptin)
Active, not recruiting
- Diabetes
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 21, 2023
Lymphangioma Trial in Albuquerque (Alpelisib)
Available
- Lymphangioma
-
Albuquerque, New MexicoUniversity of New Mexico - Cancer Center
Oct 4, 2022
Lipodystrophy, Diabetes, Hyperlipidemia Trial run by the NIDDK (Metreleptin)
Recruiting
- Lipodystrophy
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 23, 2023
Pseudoaneurysm, Carotid, Pseudoaneurysm Trial in Miami (PK Papyrus)
Temporarily not available
- Pseudoaneurysm, Carotid
- Pseudoaneurysm
- PK Papyrus
-
Miami, FloridaJackson Memorial Hospital
Jun 21, 2022
Metachromatic Leukodystrophy Trial in Durham (Enriched Hematopoetic Stem Cell Infusion)
No longer available
- Metachromatic Leukodystrophy
- Enriched Hematopoetic Stem Cell Infusion
-
Durham, North CarolinaDuke University
Jul 15, 2022
Renal Failure Trial in Chicago (Biological/Vaccine: Enriched Hematopoetic Stem Cell Infusion)
No longer available
- Renal Failure
- Biological/Vaccine: Enriched Hematopoetic Stem Cell Infusion
-
Chicago, IllinoisNorthwestern Memorial Hospital
Jul 15, 2022
Sphingomyelin Lipidosis Trial (olipudase alfa (GZ402665))
Approved for marketing
- Sphingomyelin Lipidosis
- olipudase alfa (GZ402665)
- (no location specified)
Sep 15, 2022
Relapsed or Refractory (R/R) Follicular Lymphoma (FL), DLBCL (DLBCL) Trial (Odronextamab)
Available
- Relapsed or Refractory (R/R) Follicular Lymphoma (FL)
- Diffuse Large B-Cell Lymphoma (DLBCL)
- (no location specified)
Nov 8, 2022
GERD, Gastroesophageal Reflux, Gastroparesis Trial in Kansas City (Domperidone)
Recruiting
- GERD
- +2 more
-
Kansas City, MissouriChildren's Mercy Hospitals and Clinics
May 17, 2022
Paroxysmal Nocturnal Hemoglobinuria Trial (Pozelimab, Cemdisiran)
Available
- Paroxysmal Nocturnal Hemoglobinuria
- (no location specified)
Aug 31, 2023
Malignant Tumor Trial (Experimental: DaRT seeds)
Not yet recruiting
- Malignant Tumor
- Experimental: DaRT seeds
- (no location specified)
Mar 27, 2023
Glioblastoma, High Grade Glioma, Recurrent Glioblastoma Trial in Seoul (GX-I7)
No longer available
- Glioblastoma
- +4 more
-
Seoul, Korea, Republic ofKangnam St. Mary's Hospital
Mar 2, 2022